Gio passed away a couple of years ago from a rare genetic condition called Morquio A syndrome. He spent quite a few months at ...

In 2015, NICE said that BioMarin's Vimizim could be used to treat patients with the ultra-rare disease Morquio A syndrome, while real-world data was collected on its efficacy. Now – almost seven ...

All proceeds from Scarlett’s Mini Golf Gala will directly support Scarlett’s ongoing medical care and research toward developing a cure for Morquio A Syndrome, which affects just four in 1 ...