资讯

A Gene-Editing Breakthrough Saves Infant With Rare Disease
The Crispr therapy was tailored to the baby’s specific condition and could provide a template for others.
MedPage Today on MSN1 天
In a First, CRISPR Used to Treat Infant With Ultra-Rare Disease
A tailored CRISPR base-editing therapy was given for the first time to an infant who was born with a rare genetic disease, ...
Baby Is Healed With World’s First Personalized Gene-Editing Treatment
The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...
CHOP and Penn treated an infant with a rare disease by editing his genes
A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.
Gene editing helped a desperately ill baby thrive. Scientists say it could someday treat ...
The baby, KJ Muldoon of Clifton Heights, Penn., is one of 350 million people worldwide with rare diseases, most of which are ...
Doctors save baby's life with first-ever gene fix for deadly rare disease
The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific ...
inews.co.uk on MSN1 天
Breakthrough for children with rare diseases as ‘miracle’ gene editing saves baby
A range of other rare inherited diseases are now likely to be curable by similar procedures, the research team said ...
Healio8 小时
Infant with rare disease receives world’s first personalized gene-editing therapy
An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...
Personalized CRISPR treatment used on baby with genetic disease
Doctors used personal gene therapy to treat an infant with a deadly genetic disease in a medical first. KJ Muldoon was born ...
FOX 10 Phoenix1 天
Baby born with rare disorder thrives after getting personalized gene editing treatment
Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...
Greek Reporter6 小时
US Baby Becomes First to Undergo Successful Personalized Gene Therapy
A US baby born with a rare and life-threatening genetic disease is thriving after undergoing the first successful ...
6abc Action News12 小时
Doctors save Philadelphia baby's life with first-ever gene fix for deadly rare disease
PHILADELPHIA (WPVI) -- An infant, who was born with a deadly disease, is now thriving, thanks to a medical first performed at ...