Riding recent momentum in the Duchenne muscular dystrophy space, Capricor Therapeutics, Wave Life Sciences, Regenxbio and ...

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

Research highlights that the DMD gene is the largest known human gene, featuring 79 exons (coding regions). The gene’s large size means it is prone to alterations that may result in DMD.

The DMD gene is made up of 79 exons, and mutations in that code can result in a deficiency in dystrophin which is responsible for the muscle wasting in DMD. Exon-skipping drugs are used to patch ...