A longstanding mystery in Parkinson's disease research has been why some individuals carrying pathogenic variants that ...

Investigators have developed STITCHR, a new gene editing tool that can insert therapeutic genes into specific locations without causing unwanted mutations. The system can be formulated completely as ...

Canada Gairdner Awards recognize the world’s most accomplished researchers whose work is improving our understanding of human ...

Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

A team at the Centro Nacional de Investigaciones Cardiovasculares (CNIC) has developed an innovative gene-therapy strategy ...

Swedish researchers have identified genetic variants that increase the risk of atherosclerosis. The aim is for these new ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

Three people in the rural California town of Mammoth Lakes have died from the same rare virus that killed Gene Hackman’s wife ...

Three people in a rural town in California have died from hantavirus, the rare virus that killed late actor Gene Hackman’s ...

Between 1993 and 2022, there were 864 cases of hantavirus disease in the United States. About 38% of severe infections lead ...