Breathing difficulties and heart disease usually begin by age 20. As the name suggests, Duchenne muscular dystrophy is caused by a defective gene for dystrophin (a protein in muscles). However ...

Columnist Patrick Moeschen highlights some key federal programs and pieces of legislation in the history of muscular ...

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the importance of early diagnosis of muscular dystrophy.

Duchenne muscular dystrophy (DMD ... Possible life threatening complications include respiratory problems and heart disease. Early screening can help you get a DMD diagnosis sooner and ensure ...

New Gene Therapy Reverses Heart Failure in Large Animal Model Dec ... New Gene Therapy Approach Shows Promise for Duchenne Muscular Dystrophy July 24, 2024 — Researchers have made a significant ...

Pope Francis has died​ at the age of 88 following a number of health issues in recent years. Here's what we know about his ...

many families face years of uncertainty before learning their child has a disease that silently robs them of the ability to walk, move and breathe. Children with Duchenne show no signs at birth ...

Get Instant Summarized Text (Gist) Gene therapy for Duchenne muscular dystrophy (DMD) faces challenges as the immune system may hinder its effectiveness. A large-scale trial showed that the ...

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy ... treatments that address the full scope of the disease—not just its muscle symptoms." ...