with rapid progression from congestive heart failure to death or transplantation. Dr. Jeffrey Towbin and colleagues first identified the disease-causing gene as dystrophin. Dystrophin is a ...

DMD was first described by French neurologist Guillaume Benjamin Amand Duchenne in the 1860s. However, until the 1980s, ...

A new article argues dystrophin immunogenicity is an under-examined issue in the treatment of Duchenne muscular dystrophy.

The study reveals that dystrophin's CT domain interacts differently ... which extend beyond skeletal muscles to affect organs ...

Avidity Biosciences’ Phase I/II trial of ribonucleic acid (RNA) therapy, del-zota, has increased dystrophin in patients with Duchenne muscular dystrophy (DMD). Results from the company’s ...