A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

The positive results from the second part of the EMBARK trial contrast with findings from one-year post treatment, which did ...

A new study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for understanding ...

Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...