The company said the discontinuation was due to several reasons,” Reuters news service reported, “including limited interest in gene therapies for the bleeding disorder.” (Pfizer had earlier dumped a ...

Learn how gene therapy is revolutionising the treatment of haemophilia a genetic disorder that affects blood clotting ...

Discover six hemophilia companies developing new treatments for the genetic bleeding disorder, from gene therapies to RNAi ...

Managed Healthcare Executive gives C-suite executives in health plans and provider organizations news and strategies for ...

Gene therapy marks India's first major leap in treating hemophilia * Biotechnology sector grows to over 165 billion dollars, ...

The cell and gene therapy space in recent months has hit several speedbumps, including layoffs, dropped drugs and ...

In conclusion, India’s advancement in gene therapy for hemophilia marks a transformative moment in both healthcare and biotechnology. By integrating scientific innovation with national ...

Liver-directed AAV-based gene therapy offers promise for people living with hemophilia B or other genetic disorders. 6,7,11–18 However, the long-term safety and efficacy of this approach remain ...

Single-Dose Gene Therapy Is Potentially Life-Changing for Adults With Hemophilia B Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent ...

Amid a reckoning for the gene therapy field, Vertex Pharmaceuticals has joined a growing list of companies paring back their ...

MIT engineers have designed a new method to improve the precision of gene therapy treatments by using gene circuits that ...

Many diseases are caused by a missing or defective copy of a single gene. For decades, scientists have been working on gene ...