Large-scale data analysis links rare diseases to higher COVID-19 mortality risk
An England-wide study of over 58 million people has identified eight rare diseases that carry significantly increased risks ...
EurekAlert!2d
High-quality evidence for the treatment of very rare diseases: IQWiG is involved in the EU project RealiseD
High-quality evidence for the treatment of very rare diseases: IQWiG is involved in the EU project RealiseD Developing clinical trials to provide good evidence for very rare diseases, so that ...
pharmaphorum11h
Exploring the future: Opportunities and challenges in cell and gene therapy for rare diseases
In this webinar, sponsored by IPG Health, we will explore the role that cell and gene therapies can play in treating rare diseases, the unique challenges faced by pharmaceutical companies, healthcare ...
MDA Launches 75th Anniversary Campaign and Premieres New PSA to Shine a Light on Rare Diseases
Celebrating 75 Years of Progress, Legacy, Impact, and Momentum Leading up to Rare Disease Day on February 28 Muscular ...