资讯

Nature1 年
A cure for sickle cell disease is taking shape
When asked to picture the ideal cure for sickle-cell disease, molecular biologist Stefano Rivella, a researcher at Children’s Hospital of Philadelphia (CHOP), Pennsylvania, didn’t gaze into ...
Nature4 年
One-time gene therapy for sickle cell disease
Aruvant is developing ARU-1801, a one-time, potentially curative gene therapy for sickle cell disease and β-thalassemia. In an ongoing clinical phase 1/2 study, ARU-1801, administered with only ...
BBC28 天
Sickle cell patients not listened to - report
The findings were part of a research project commissioned by London Ambulance Service (LAS) NHS Trust and carried out by the Sickle Cell Society. LAS said it had developed an action plan to ...
来自MSN28 天
Oral Chemotherapy Drug Shows Long-Term Benefits For Children With Sickle Cell Disease
A new study has found that an oral drug called hydroxyurea can safely and effectively treat children with sickle cell disease. The research was published on April 17 in the medical journal Blood ...
St. Louis Post-Dispatch22 天
In a first for St. Louis, patient completes new gene therapy to cure sickle cell disease
Cancel anytime. Martin Mwita and his mother Jacinta Mwita, both of Omaha, speak about his journey living with sickle cell disease and receiving treatment from St. Louis Children’s Hospital on ...
Post and Courier25 天
Robert F. Kennedy Jr. unveils sickle cell treatment push during Charleston visit
Kennedy Jr. announced a landmark initiative to expand access to cutting-edge treatments for sickle cell disease, a genetic blood disorder that disproportionately affects Black Americans ...