Gene therapy, a technique that is revolutionizing ... groups who were brought together under Phase I of the NIH's Somatic Cell Genome Editing Consortium. More information: Christopher J.

If administered early, gene therapy has the potential to change the medical history of children born with metachromatic ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

NEW YORK – In cell and gene therapies, the genetic machinery is key to producing the proteins missing or dysregulated in a disease, but whether the therapeutic cassette reaches target cells and how ...

Hematopoietic stem cell gene therapy (HSC-GT) represents a cutting ... stress were found to modulate HSC activity and somatic mutation rates. The detailed insights the findings provide have ...

Human gene therapy involves the insertion of DNA (or RNA) into somatic cells to produce a therapeutic effect. Gene therapy was first envisaged as an approach to treating genetic disorders. In this ...

Join us for an insightful webinar on the latest advancements in cell and gene therapy, focusing on the innovative Cas9-CLIPT technology. Cas9-CLIPT (Cleaved, Linearized with Protein Template ...