The determination comes after recruitment and dosing in certain trials were paused after a young patient died due to acute ...

Columnist Patrick Moeschen, anticipating his own historic anniversary, celebrates champions of the disability rights movement ...

DMD treatment KER-065 showed a good safety profile in a Phase 1 clinical trial with no serious side effects seen in healthy ...

Betty Vertin, mother of three sons with Duchenne, shares her journey of managing treatment, mental health, and parenting ...

Hawkin Miller, who has Duchenne muscular dystrophy, shares motivation and advice for staying on track with treatment.

Treatment with gene therapy candidate BB-301 led to improvements in swallowing ability for the first three OPMD patients in a ...

Shalom Lim, who has Duchenne muscular dystrophy, shares how caregivers can support patient autonomy when it comes to ...

Health Canada granted priority review to an application seeking approval of vamorolone, marketed in the U.S. as Agamree, for Duchenne MD.

Rob Stemple is a lifelong advocate for people with disabilities. He was diagnosed with FSHD in 1971 at age 14. Rob struggled with its’ affects for over 50 years. He lost his eyesight in a devastating ...

When living with Duchenne muscular dystrophy, taking a gamble feels better than not doing anything at all, columnist Betty Vertin writes.

Betty Vertin is a mother and writer living in rural Hastings, Nebraska, with her husband and seven children. Betty is a caregiver to three sons, Max, Rowen, and Charlie. Her oldest was diagnosed with ...