Researchers combined advanced imaging techniques and theoretical physics to observe and explain how nanoclusters of the protein emerin form inside living cells. The study uncovers the molecular 'rules ...

Building your Duchenne MD care team, with specialists such as a neurologist, cardiologist, and physical therapist, is ...

GenAssist’s IND application for GEN6050X receives US FDA clearance, a globally first-in-class base editing drug for duchenne muscular dystrophy: Suzhou, China Friday, March 7, 2 ...

The Minnesota Department of Health has officially added two more diseases to the list of conditions for which newborns are ...

Italfarmaco S.p.A. today announced a comprehensive update on the regulatory and clinical advancements for givinostat, the ...

ITF Therapeutics LLC, the U.S. affiliate of Italfarmaco, today announced the opening of the company's new U.S. headquarters in Concord, Massachusetts. The 10,000-square-foot facility located at 575 ...

Capricor Therapeutics, Inc.'s Deramiocel receives FDA Priority Review for DMD cardiomyopathy, with a decision by Aug. 2025.

Sarepta Therapeutics hits 52-week lows despite strong earnings and growth. Read why investors should view SRPT as a high risk ...

A grandmother is raising awareness of a severe muscle-wasting disease after her grandson was diagnosed with it ...

The Minnesota Department of Health’s Newborn Screening Program is checking for Duchenne muscular dystrophy and ...

MDH says early identification and treatment are crucial to slowing the progression of symptoms, as well as improving the ...