None of the eteplirsen-treated patients reached a left ventricular ejection fraction below 50% compared with 22.1% of ...

Blood pressure and heart rate (pulse) are two important vital signs measured during a healthcare visit. Blood pressure (BP) is a measure of the force of blood on the blood vessel walls. Blood vessels ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...

New Study Investigates Effects of ADHD Medications on the Heart Apr. 7, 2025 — A new study has found that medications for ADHD have overall small effects on blood pressure and heart rate after ...

Sarepta Therapeutics, Inc. , the leader in precision genetic medicine for rare diseases, today shared updates from its clinical programs focused on limb-girdle muscular dystrophy (LGMD) subtypes 2C/R5 ...

Its DELIVER platform generates capsids that are designed to avoid the liver and target muscle and heart cells ... and more uniform expression of the dystrophin protein deficient in the disease ...

Sarepta's gene therapy – like rivals from Pfizer and Solid Biosciences – codes for a shortened form of the dystrophin protein ... inflammation of the heart muscle – that was seen in an ...

Keros Therapeutics halted phase 2 of TROPOS, but KER-065 shows promise in DMD and financial stability ensures growth ...

The current cash prize £10,000! This time last year we changed Heart listener Samantha Hayes's life forever, when she won £1 million in Heart's Make Me a Millionaire. And in 2025 we're doing it ...

Orca-T showed lower rates of graft-vs-host disease or infection compared with allogeneic hematopoietic stem cell transplantation for myelodysplastic syndrome (MDS) or acute leukemias in the ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in cells. The company plans to begin a pivotal trial next year.

Department of Cardiology, Center for Translational and Experimental Cardiology, University Hospital Zurich, University of Zurich, Switzerland. (S.C., S.A.M., S.A., M ...