As we continue to see sequencing technologies advance and provide a deeper understanding of gene therapy targets along with ...

For patients with disorders such as autism and schizophrenia, mutations in the same gene could require different treatments, ...

Failure of a gene-reading quality-control mechanism called Integrator leaves cells littered with abnormal RNA strands that ...

An 11-year-old from Rowlett is set to make medical history as the first person in the world to receive treatment for NARS1.

Opus Genetics, Inc. (Nasdaq: IRD), a clinical-stage ophthalmic biotechnology company developing gene therapies for the ...

David Murphy discovered one of his calves had three hooves on each of its front feet. This genetic defect is called ...

Scientists from the Garvan Institute of Medical Research have discovered that certain gene changes linked to leukemia may ...

Sensorion (FR0012596468 ALSEN) a pioneering clinical-stage biotechnology company specializing in the development of novel therapies to restore, treat and prevent hearing loss disorders ...

KRAS-targeted therapies, including daraxonrasib and zoldonrasib, show promise in overcoming resistance in cancer treatment, ...

Failure of a gene-reading quality-control mechanism called Integrator leaves cells littered with abnormal RNA strands that ...