Scientists at Rady Children's Institute for Genomic Medicine, and the Department of Neurosciences and Pediatrics at the ...

Mpox, once a rare virus mainly confined to parts of Central Africa, is rapidly evolving into a more serious global health ...

Researchers harness the power of the world’s most advanced supercomputers to simulate the inner workings of cellular ...

Immunodeficiency disorders linked to cytoskeleton defects are rare and complex, often presenting with diverse clinical features.

UCLA Health researchers say study findings uncover Huntington's disease mechanisms and pave new ways to develop treatments.

Base editing corrected a mutation that causes macular degeneration, highlighting the potential of gene therapy to treat ...

That mad scientist who created designer babies is, apparently, gearing up for more human gene-hacking research.

Deep-sea fish adapt to some of the most extreme conditions on Earth. New research analyzing their evolution finds the same ...

Marek’s disease can be pervasive in chicken houses. Chickens infected by this highly contagious viral disease often develop ...

Researchers have revealed a secret behind horses' exceptional endurance – a mutation in the KEAP1 gene that boosts energy production while protecting against cellular oxidative stress. The findings – ...

Congenital hearing loss refers to impaired auditory function that occurs due to genetic causes. GJB2 is the gene responsible ...

AIRNA’s lead candidate AIR-001 works by correcting the most common pathologic mutation driving the rare disease alpha-1 ...