For DMD caregivers and people with Duchenne, knowing the early signs and next steps can improve self-care and help manage a ...

Italfarmaco S.p.A. today announced a comprehensive update on the regulatory and clinical advancements for givinostat, the ...

The Minnesota Department of Health has officially added two more diseases to the list of conditions for which newborns are ...

Duchenne muscular dystrophy (DMD) is a severe and progressive ... soon as possible and can also teach you what warning signs and symptoms to watch for when you’re on your own.

An FDA decision on deramiocel for heart muscle disease in DMD is now expected by Aug. 31, after its application was granted ...

Researchers, physicians, families and affected patients view Duchenne muscular dystrophy (DMD) as a neuromuscular condition. Children are diagnosed during the first years of life because they have ...

There is a broad consensus in the medical community in support of Duchenne newborn screening and we in Connecticut are hoping ...

Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in the ...

GenAssist’s IND application for GEN6050X receives US FDA clearance, a globally first-in-class base editing drug for duchenne muscular dystrophy: Suzhou, China Friday, March 7, 2 ...

—Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in ...

Duchenne muscular dystrophy (DMD) is caused by mutations in the dystrophin gene, leading to muscle degeneration. Current treatments focus on maintaining muscle function, with emerging gene ...

Researchers combined advanced imaging techniques and theoretical physics to observe and explain how nanoclusters of the protein emerin form inside living cells. The study uncovers the molecular 'rules ...