Edgewise Therapeutics , Inc. (NASDAQ:EWTX), with a market capitalization of $2.67 billion, is a biopharmaceutical company focused on developing innovative therapies for severe, rare muscle disorders.

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

该研究也指出，由于DMD突变类型多样且分布广泛，单一ASO药物难以覆盖所有患者。尤其是针对深层内含子突变的修复，现有方法的效果仍然有限。此外，基因治疗的研发成本高昂，临床转化周期长，给患者的普及使用带来显著障碍。

Certain types, including Duchenne muscular dystrophy, can lead to problems with the heart and muscles used for breathing. Some people with MD may develop other life-threatening complications as well, ...

Zocor (simvastatin) and Lipitor (atorvastatin) are both statin drugs, which are medications used to lower cholesterol levels in the blood. Statins primarily work by inhibiting the enzyme HMG-CoA ...

As COO, Dr. Derakhshan will be responsible for enabling the operational readiness of the organization as the Company approaches significant milestones in the muscular dystrophy and cardiovascular ...

Thanks to the success against Paul today, Alexander overtook his compatriot Boris Becker for the most victories in Melbourne (30) and claimed his 106th Grand Slam tournament victory (surpassing ...

A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and inflammation.

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early diagnosis, multidisciplinary care, and emerging treatments like gene therapy ...

Karun Nair's exploits in the Vijay Hazare Trophy was on Friday termed "nothing short of extraordinary" by batting legend Sachin Tendulkar, who urged the Vidarbha skipper to "keep going." Nair has been ...

West Indies had about 15 overs to face before lunch, and Pakistan just about made victory safe in this time. The visitors began with positive intent, having realised that poking and prodding would ...