RAG-17 therapy slowed functional decline and stabilized or improved breathing in people with ALS who carry mutations in the SOD1 gene.

But a new genetic test appears capable of sussing out which men are at greater risk of urinary side effects from radiation ...

The CAR T-cell therapy KYV-101 is safe, and showed preliminary signs of efficacy in patients with progressive forms of MS in ...

The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug ...

Global Clinical Trial Expansion and Rising Chronic Disease Burden Fuel Demand for Specialized CRO ServicesDublin, April 15, 2025 (GLOBE NEW ...

Sickle cell disease, characterised by the abnormal sickle shape of red blood cells instead of the typical round form, is the UK's most rapidly expanding genetic disorder. This deformation causes ...

Calvin Campbell lost all the flesh on his legs and was paralysed for months because of an agonising disease that's the fastest growing genetic condition in the UK ...

Signs of Type 5 diabetes can vary depending on the subtype but usually include: Mild to moderate elevated blood glucose ...

INmune Bio (INMB) has partnered with the Cell and Gene Therapy Catapult to establish large-scale, commercial-ready manufacturing for its cell ...

USA Fencing has acknowledged a forthcoming federal investigation into an incident that occurred at one of its events where a ...

The gene therapy BBM-H901 (dalnacogene ponparvovec) has been approved in China for adults with moderate to severe hemophilia ...