From Washington to Wall Street, it's a crazy time for biotech. But as Ultragenyx Pharmaceutical Inc. celebrates its 15th ...

In today’s fast-paced world, maintaining optimal health has become a primary concern for many individuals. Diet and exercise ...

Ultragenyx's strong revenue growth, diverse streams, and late-stage pipeline make it a standout in rare disease and gene ...

Certain foods can be bad for your health if you have kidney disease. Avoiding or limiting foods high in sodium, potassium, and phosphorus when you have kidney disease can help slow or stop disease ...

Purpose: Infantile glycogen storage disease type II (GSD-II) is a fatal genetic muscle disorder caused by deficiency of acid α-glucosidase (GAA). The purpose of this study was to investigate the ...

Assmann G, Seedorf U. Acid lipase deficiency: Wolman disease and cholesterol ester storage disease. Sciver CR, Beuadet LA, Sly WS, Valle D. The Metabolic & Molecular Bases of Inherited Disease (8th ...

CRISPR can't target every location in the genome, and it can't fix the thousands of mutations present in diseases like cystic fibrosis," said co-senior author Omar Abudayyeh, Ph.D., an ...

"Treatment for mitochondrial diseases within reach." ScienceDaily. www.sciencedaily.com / releases / 2025 / 04 / 250409114701.htm (accessed April 22, 2025). Explore More ...

DOGE recently posted on X to claim it had made progress in persuading the IT team at the US General Services Administration (GSA) to save "$1 million per year by converting 14,000 magnetic tapes ...

‘A 17th-century pirate disease,’ Robbie told The Mirror. He added that he was getting incredibly thin, but his body dysmorphia made concerned comments from friends and family sound like ...

Symptoms of some of the diseases that mimic lung cancer, such as asthma or acid reflux, are common with many conditions. They can include persistent cough, chest pain, shortness of breath, unexplained ...

Kennedy offered his own answer: “chronic disease,” to which “90 percent of health-care spending” is devoted. He specifically pointed to rising rates of obesity, diabetes, and cancer, as well as ...