US infant KJ Muldoon makes history as first patient treated with personalized gene-editing, offering hope for rare illnesses.

Americans judge transplant candidates based on perceived personal responsibility, with the least support given to those seen ...

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KJ Muldoon was born with a rare, potentially fatal genetic disorder, but instead of a liver transplant, he was able to be ...

Researchers used CRISPR gene-editing tech to create the first successful bespoke drug, aimed at treating a newborn's rare ...

“This is the first step towards the use of gene editing therapies to treat a wide variety of rare genetic disorders for which ...

The child will need to be monitored throughout his life, but researchers said the treatment’s success indicates that other ...

KJ Muldoon became the first patient to undergo personalized CRISPR treatment, a therapy that found the one uniquely mutated gene out of 20,000 in his little body, and fixed it.

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

Simultaneous liver transplant and sleeve gastrectomy yield durable weight loss, resolution of diabetes and hypertension, and a reduction in allograft steatosis development.